APRTX 004
Alternative Names: APRTX-004Latest Information Update: 20 Jan 2026
At a glance
- Originator Aperture Therapeutics
- Class Oligonucleotides
- Mechanism of Action Gene silencing; Protein expression modulators
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Research Peripheral neuropathies
Most Recent Events
- 19 Dec 2025 Early research in Peripheral neuropathies in USA (unspecified route) prior to December 2025 (Aperture Therapeutics pipeline, December 2025)