SRNDC 03
Alternative Names: SRNDC-03Latest Information Update: 13 Feb 2026
At a glance
- Originator Sirius Therapeutics
- Class Coagulants; Small interfering RNA
- Mechanism of Action RNA interference
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Blood coagulation disorders
Most Recent Events
- 22 Jan 2026 Preclinical trials in Blood coagulation disorders in USA (unspecified route) (Sirius Therapeutics pipeline; January 2026)