SRNDO 05
Alternative Names: SRNDO-05Latest Information Update: 13 Feb 2026
At a glance
- Originator Sirius Therapeutics
- Class Small interfering RNA
- Mechanism of Action RNA interference
-
Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Muscular atrophy
Most Recent Events
- 31 Jan 2026 Preclinical trials in Muscular atrophy in USA (IM) (Sirius Therapeutics pipeline; January 2026)