Research programme: Transthyretin amyloid depleter antibody - BridgeBio Pharma
Alternative Names: Transthyretin amyloid depleter antibody; TTR amyloid depleter; TTR amyloid depleter antibodyLatest Information Update: 05 Mar 2026
At a glance
- Originator BridgeBio Pharma
- Class Monoclonal antibodies
- Mechanism of Action Amyloid modulators; Prealbumin modulators
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Research Transthyretin-related hereditary amyloidosis
Most Recent Events
- 25 Feb 2026 BridgeBio Pharma announces intention to submit IND to the US FDA in 2027
- 25 Jan 2026 Early research in Transthyretin-related hereditary amyloidosis in USA (Parenteral), before January 2026
- 12 Jan 2026 BridgeBio Pharma plans clinical trials for the treatment of Transthyretin amyloid cardiomyopathy in 2027-2028