Research programme: Small interfering RNA therapeutics - Sirius Therapeutics
Latest Information Update: 13 Feb 2026
At a glance
- Originator Sirius Therapeutics
- Class Small interfering RNA
- Mechanism of Action RNA interference
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical CNS disorders
Most Recent Events
- 27 Jan 2026 Preclinical trials in CNS disorders in USA (Intracerebral) (Sirius Therapeutics pipeline; January 2026)