CHF REXBBB 02
Alternative Names: CHF-REXBBB-02Latest Information Update: 09 Feb 2026
At a glance
- Originator Key2Brain
- Developer Chiesi Global Rare Diseases; Key2Brain
- Class Enzymes; Neuroprotectants; Recombinant proteins
- Mechanism of Action Galactosylceramidase replacements
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Globoid cell leukodystrophy
Most Recent Events
- 30 Jan 2026 Preclinical trials in Globoid cell leukodystrophy in Italy (unspecified route), prior to January 2026 (Chiesi Global Rare Diseases pipeline, January 2026)
- 30 Jan 2026 Preclinical trials in Globoid cell leukodystrophy in Sweden (unspecified route), prior to January 2026 (Chiesi Global Rare Diseases pipeline, January 2026)
- 11 Jun 2025 CHF REXBBB 02 licensed to Chiesi Global Rare Diseases worldwide