CTX 1000
Alternative Names: AAV9 gene therapy - Celosia Therapeutics; CTX-1000Latest Information Update: 20 Feb 2026
At a glance
- Originator Celosia Therapeutics
- Class Antidementias; Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase I Amyotrophic lateral sclerosis
- Preclinical Frontotemporal dementia
Most Recent Events
- 20 Feb 2026 Celosia Therapeutics plans to files an IND application for the first in patient trial for Amyotrophic lateral sclerosis (ADNM)
- 12 Feb 2026 Preclinical trials in Frontotemporal dementia in Australia (Intracisternal) (Celosia Therapeutics pipeline, February 2026)
- 12 Feb 2026 Prior to February 2026, Celosia Therapeutics plans to files an IND application for the first in patient trial for Amyotrophic lateral sclerosis in third quarter 2025(Celosia Therapeutics pipeline, February 2026)