AAV PQBP1 gene therapy - Change Cure
Alternative Names: AAV-PQBP1Latest Information Update: 28 Apr 2026
At a glance
- Originator Change Cure
- Class Antidementias; Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Research Alzheimer's disease
Most Recent Events
- 17 Feb 2026 Early research in Alzheimer's disease in Japan (Parenteral), prior to February 2026 (Change Cure pipeline, February 2026)