Macular degeneration gene therapy - MeiraGTx
Latest Information Update: 23 Feb 2026
At a glance
- Originator MeiraGTx
- Class Eye disorder therapies; Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Age-related macular degeneration; Dry macular degeneration
Most Recent Events
- 23 Feb 2026 Preclinical trials in Age-related macular degeneration in USA (Parenteral), prior to February 2026 (MeiraGTx's pipeline, February 2026)
- 23 Feb 2026 Preclinical trials in Dry macular degeneration in USA (Parenteral), prior to February 2026 (MeiraGTx's pipeline, February 2026) (MeiraGTx's pipeline, February 2026)