CTX 321
Alternative Names: CTX-321Latest Information Update: 12 Mar 2026
At a glance
- Originator CRISPR Therapeutics
- Class Antihyperlipidaemics; Gene therapies
- Mechanism of Action Gene expression inhibitors; Lipoprotein A expression inhibitors
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Hyperlipidaemia