ENTDMD 001
Alternative Names: ENTDMD-001Latest Information Update: 27 Feb 2026
At a glance
- Originator Entos Pharmaceuticals
- Class Gene therapies
- Mechanism of Action Dystrophin replacements; Gene transference
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Research Duchenne muscular dystrophy
Most Recent Events
- 27 Feb 2026 Early research in Duchenne muscular dystrophy in Canada (Parenteral), before February 2026 (Entos Pharmaceuticals pipeline, February 2026)