DYNE 255
Alternative Names: DYNE-255Latest Information Update: 11 Mar 2026
At a glance
- Originator Dyne Therapeutics
- Class Antibodies; Antisense oligonucleotides; Drug conjugates; Immunoconjugates
- Mechanism of Action Dystrophin expression stimulants; Gene silencing
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Duchenne muscular dystrophy