Drug Profile

SRP 1007

Alternative Names: SRP-1007

Latest Information Update: 20 Mar 2026

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At a glance

Originator Sarepta Therapeutics
Class Drug conjugates; Immunoconjugates; Immunoglobulin fragments; Small interfering RNA
Mechanism of Action RNA interference

Orphan Drug Status

Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

No
New Molecular Entity Yes

03 Mar 2026 Preclinical development in Spinocerebellar ataxias in USA (Parenteral)

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