SRP 1006
Alternative Names: SRP-1006Latest Information Update: 20 Mar 2026
At a glance
- Originator Sarepta Therapeutics
- Class Drug conjugates; Immunoconjugates; Immunoglobulin fragments; Small interfering RNA
- Mechanism of Action RNA interference
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Machado-Joseph Disease