GenSci 124
Alternative Names: GenSci-124Latest Information Update: 27 Mar 2026
At a glance
- Originator GeneScience Pharmaceuticals
- Class Antifibrotics; RNA
- Mechanism of Action Cystic fibrosis transmembrane conductance regulator expression stimulants
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Phase Unknown Cystic fibrosis
Most Recent Events
- 27 Mar 2026 Investigation in Cystic fibrosis in China (Inhalation) (GeneScience Pharmaceuticals pipeline, March 2026)