CTX 001 - Cajal Therapeutics
Alternative Names: CTX-001 - Cajal TherapeuticsLatest Information Update: 07 Apr 2026
At a glance
- Originator Cajal Therapeutics
- Class Antianaemics; Small molecules
- Mechanism of Action Iron modulators
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Anaemia; Unspecified
Most Recent Events
- 06 Apr 2026 Preclinical trials in Anaemia in USA (PO), before April 2026 (Cajal Therapeutics pipeline, April 2026)
- 06 Apr 2026 Preclinical trials in Unspecified in USA (PO), before April 2026 (Cajal Therapeutics pipeline, April 2026)
- 06 Apr 2026 Cajal Therapeutics plans a phase I trial in Anaemia (PO) in the first half of 2026 (Cajal Therapeutics pipeline, April 2026)