Iron mobiliser for CNS disorder - Cajal Therapeutics
Latest Information Update: 07 Apr 2026
At a glance
- Originator Cajal Therapeutics
- Class Antiparkinsonians; Small molecules
- Mechanism of Action Iron modulators
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Friedreich's ataxia; Parkinson's disease
Most Recent Events
- 06 Apr 2026 Preclinical trials in Friedreich's ataxia in USA (unspecified route), before April 2026 (Cajal Therapeutics pipeline, April 2026)
- 06 Apr 2026 Preclinical trials in Parkinson's disease in USA (unspecified route), before April 2026 (Cajal Therapeutics pipeline, April 2026)