CTX 2000
Alternative Names: CTX-2000Latest Information Update: 22 Apr 2026
At a glance
- Originator Celosia Therapeutics
- Class Gene therapies; Neuroprotectants
- Mechanism of Action Gene transference; Proteolysis
-
Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Amyotrophic lateral sclerosis
Most Recent Events
- 08 Apr 2026 Preclinical trials in Amyotrophic lateral sclerosis in Australia (Parenteral), prior to April 2026 (Celosia Therapeutics pipeline, April 2026)
- 08 Apr 2026 Celosia Therapeutics plans clinical trials for Amyotrophic lateral sclerosis (Parenteral) (Celosia Therapeutics pipeline, April 2026)
- 26 Aug 2025 Celosia Therapeutics has patent protection for CTX 2000 in USA, Australia and China