RAI 001
Alternative Names: RAI-001Latest Information Update: 13 Apr 2026
At a glance
- Originator Receptor.AI
- Class Small molecules; Urologics
- Mechanism of Action Ion channel modulators
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Kidney disorders
Most Recent Events
- 13 Apr 2026 Pharmacodynamics and adverse event data from the preclinical trial released by Receptor.AI (Receptor.AI website; April 2026)
- 13 Apr 2026 Receptor.AI plans proof-of-concept studies for Kidney disorders (Receptor.AI website; April 2026)
- 10 Apr 2026 Preclinical trials in Kidney disorders in USA (PO) prior to April 2026 (Receptor.AI pipeline; April 2026)