GT 04686
Alternative Names: GT-04686Latest Information Update: 30 Apr 2026
At a glance
- Originator Gain Therapeutics
- Class Antiparkinsonians; Small molecules
- Mechanism of Action Glucosylceramidase modulators
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Parkinson's disease