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BEAM 304

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Drug Profile

BEAM 304

Alternative Names: BEAM-304

Latest Information Update: 12 Apr 2026

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At a glance

  • Originator Beam Therapeutics
  • Class Gene therapies
  • Mechanism of Action Gene transference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    No
  • New Molecular Entity No

Highest Development Phases

  • Preclinical Phenylketonuria

Most Recent Events

  • 24 Feb 2026 Preclinical trials in Phenylketonuria in USA (IV), prior to February 2026 (Beam Therapeutics pipeline, March 2026)
  • 24 Feb 2026 Pharmacodynamics data from preclinical trial in Phenylketonuria released by Beam Therapeutics
  • 24 Feb 2026 Beam plans phase I/II clinical trial in Phenylketonuria

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