Bone Marrow Stem Cell Transplantation for Children With Stem Cell Defects, Marrow Failure Syndromes, or Myeloid Leukemia in 1Remission
Latest Information Update: 10 Apr 2025
At a glance
- Drugs Antithymocyte globulin (Primary) ; Busulfan (Primary) ; Fludarabine (Primary)
- Indications Acute myeloid leukaemia; Aplastic anaemia; Beta-thalassaemia; Blood dyscrasias; Bone marrow disorders; Chronic myeloid leukaemia; Diamond-Blackfan syndrome; Sickle cell anaemia; Wiskott-Aldrich syndrome
- Focus Therapeutic Use
Most Recent Events
- 12 Oct 2006 New trial record.