Effects and health economic aspects of enzyme therapy in children and adults with Pompe disease Long-term follow-up of patients receiving commercially available Myozyme.
Phase of Trial: Phase IV
Latest Information Update: 23 Aug 2011
At a glance
- Drugs Alglucosidase alfa (Primary)
- Indications Glycogen storage disease type II
- Focus Therapeutic Use
- 23 Aug 2011 New trial record