A Phase I Study of the Safety and Preliminary Effectiveness of Human CNS Stem Cells (HuCNS-SC) in Patients With Neuronal Ceroid Lipofuscinosis Caused by Palmitoyl Protein Thioesterase 1 (PPT1) or Tripeptidyl Peptidase 1 (TPP-I) Deficiency
Latest Information Update: 07 Nov 2021
At a glance
- Drugs Adult neural stem cells (Primary)
- Indications Neuronal ceroid lipofuscinosis
- Focus Adverse reactions
- Sponsors StemCells
- 11 Oct 2013 New trial record