A Phase 3, Randomized, Double-Blind, Placebo-Controlled, Multinational Clinical Study to Evaluate the Efficacy and Safety of 2.0 mg/kg/Week and 2.0 mg/kg/Every Other Week BMN 110 in Patients With Mucopolysaccharidosis IVA (Morquio A Syndrome)
Latest Information Update: 12 Jan 2022
Price :
$35 *
At a glance
- Drugs Elosulfase alfa (Primary)
- Indications Mucopolysaccharidosis IV
- Focus Registrational; Therapeutic Use
- Sponsors BioMarin Pharmaceutical
- 01 Nov 2014 Primary endpoint (Change From Baseline in Endurance as Measured by the 6-minute Walk Test) has been met as results published in the Journal of Inherited Metabolic Disease
- 26 Feb 2014 New trial record