A Phase 2a Study of Ataluren (PTC124) in Nonambulatory Patients With Nonsense-Mutation-Mediated Duchenne/Becker Muscular Dystrophy
Latest Information Update: 07 Nov 2021
At a glance
- Drugs Ataluren (Primary)
- Indications Duchenne muscular dystrophy
- Focus Adverse reactions
- Sponsors PTC Therapeutics
- 02 Apr 2014 New source identified and integrated (European Clinical Trials Database; EudraCT2009-013169-24).
- 01 Apr 2014 New trial record
- 03 Mar 2010 Status changed from recruiting to discontinued, according to ClinicalTrials.gov.