A Phase II Randomized Controlled Study of Miglustat in Adult and Juvenile Patients With Niemann-Pick Type C Disease
Latest Information Update: 04 Apr 2014
At a glance
- Drugs Miglustat (Primary)
- Indications Niemann-Pick disease type C
- Focus Pharmacodynamics
- Sponsors Actelion Pharmaceuticals
Most Recent Events
- 04 Apr 2014 New trial record
- 09 May 2009
- 22 Jul 2008