A Phase II Randomized Controlled Study of Miglustat in Adult and Juvenile Patients With Niemann-Pick Type C Disease
Latest Information Update: 04 Apr 2014
Price :
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At a glance
- Drugs Miglustat (Primary)
- Indications Niemann-Pick disease type C
- Focus Pharmacodynamics
- Sponsors Actelion Pharmaceuticals
- 04 Apr 2014 New trial record
- 09 May 2009
- 22 Jul 2008