Treatment of Early Infantile-Onset Lysosomal Storage Diseases With Fetal Umbilical Cord Blood (UCB) Transplantation
Status: Withdrawn prior to enrolment
Phase of Trial: Phase I
Latest Information Update: 06 Apr 2017
Price : $35 *
At a glance
- Drugs ALD 601 (Primary)
- Indications Gangliosidoses; Globoid cell leukodystrophy; GM2 gangliosidoses; Metachromatic leukodystrophy; Pelizaeus-Merzbacher disease; Tay-Sachs disease
- Focus Adverse reactions; Therapeutic Use
- 31 Aug 2018 Biomarkers information updated
- 03 Apr 2017 Planned End Date changed from 1 Dec 2017 to 1 Mar 2017.
- 03 Apr 2017 Planned primary completion date changed from 1 Dec 2017 to 1 Mar 2017.