Trial Profile
Phase I Clinical Study of AAV1-gamma-sarcoglycan Gene Therapy for Limb Girdle Muscular Dystrophy Type 2C
Status:
Completed
Phase of Trial:
Phase I
Latest Information Update: 07 Nov 2021
Price :
$35
*
At a glance
- Drugs AAV1-gSG (Primary)
- Indications Limb girdle muscular dystrophies; Sarcoglycanopathies
- Focus Adverse reactions
- Sponsors Genethon
- 05 May 2014 tidied drug term in text and treatment table
- 22 Apr 2014 New trial record