Phase I/II Gene Transfer Clinical Trial of rAAV9.CMV.hNAGLU for Mucopolysaccharidosis (MPS) IIIB
Latest Information Update: 17 May 2022
At a glance
- Drugs ABO-101 (Primary)
- Indications Mucopolysaccharidosis III
- Focus Adverse reactions; First in man; Therapeutic Use
- Acronyms Transpher B
- Sponsors Abeona therapeutics
- 29 Apr 2022 Status changed from active, no longer recruiting to discontinued.
- 21 Apr 2022 This trial has been discontinued in Germany.
- 02 Dec 2021 This trial has been discontinued in Spain, according to European Clinical Trials Database record.