Phase I/II Gene Transfer Clinical Trial of scAAV9.U1a.hSGSH for Mucopolysaccharidosis (MPS) IIIA

Trial Profile

Phase I/II Gene Transfer Clinical Trial of scAAV9.U1a.hSGSH for Mucopolysaccharidosis (MPS) IIIA

Recruiting
Phase of Trial: Phase I/II

Latest Information Update: 07 Mar 2018

At a glance

  • Drugs ABO 102 (Primary)
  • Indications Mucopolysaccharidosis III
  • Focus Adverse reactions; First in man
  • Sponsors Abeona therapeutics
  • Most Recent Events

    • 08 Feb 2018 According to an Abeona Therapeutics media release, results from this study were presented at the WORLDSymposium for Lysosomal Diseases meeting.
    • 08 Feb 2018 Results published in the Abeona therapeutics Media Release.
    • 02 Feb 2018 According to an Abeona Therapeutics media release, data will be presented at the 14th Annual WORLDSymposium meeting.
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