A Safety Confirmatory Study of JC0498 (Laronidase) in Mucopolysaccharidosis I (MPS I) Patients
Latest Information Update: 06 Nov 2021
At a glance
- Drugs Laronidase (Primary)
- Indications Mucopolysaccharidosis I
- Focus Adverse reactions
- Sponsors Genzyme Corporation
Most Recent Events
- 06 Jun 2014 New trial record