A Safety Confirmatory Study of JC0498 (Laronidase) in Mucopolysaccharidosis I (MPS I) Patients
Latest Information Update: 06 Nov 2021
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At a glance
- Drugs Laronidase (Primary)
- Indications Mucopolysaccharidosis I
- Focus Adverse reactions
- Sponsors Genzyme Corporation
- 06 Jun 2014 New trial record