A Phase I/II Safety, Tolerability, Ascending Dose and Dose Frequency Study of Recombinant Human Heparan N-Sulfatase (rhHNS) Intrathecal Administration Via an Intrathecal Drug Delivery Device in Patients With Sanfilippo Syndrome Type A (MPS IIIA)

Status: Completed

Phase of Trial: Phase I/II

Latest Information Update: 06 Nov 2021

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At a glance

Drugs SHP 610 (Primary)
Indications Mucopolysaccharidosis III
Focus Adverse reactions; First in man; Therapeutic Use
Sponsors Shire; Shire Human Genetic Therapies

Most Recent Events

18 Jul 2019 This trial has been completed in United Kingdom, according to European Clinical Trials Database
25 Jun 2014 New trial record

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