A Phase 2 Study of PTC124 as an Oral Treatment for Nonsense-Mutation-Mediated Cystic Fibrosis.
Latest Information Update: 17 Sep 2021
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At a glance
- Drugs Ataluren (Primary)
- Indications Cystic fibrosis
- Focus Pharmacogenomic; Therapeutic Use
- Sponsors PTC Therapeutics
- 07 Aug 2014 New trial record