Trial Profile

Pilot and Feasibility Study of Hematopoietic Stem Cell Gene Transfer for the Wiskott-Aldrich Syndrome

Status: Completed

Phase of Trial: Phase I/II

Latest Information Update: 28 Apr 2025

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At a glance

Drugs WASp gene therapy (Primary)
Indications Wiskott-Aldrich syndrome
Focus Adverse reactions; Therapeutic Use

Most Recent Events

23 Apr 2025 Status changed from active, no longer recruiting to completed.
17 Jun 2024 Planned End Date changed from 1 Jul 2024 to 1 Aug 2024.
17 Jun 2024 Planned primary completion date changed from 1 Jul 2024 to 1 Aug 2024.

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