Trial Profile
Hydroxypropyl Beta Cyclodextrin for Niemann-Pick Type C1 Disease
Status:
Completed
Phase of Trial:
Phase I/II
Latest Information Update: 06 Nov 2021
Price :
$35
*
At a glance
- Drugs Adrabetadex (Primary)
- Indications Niemann-Pick disease type C
- Focus Pharmacokinetics
- Sponsors Vtesse
- 11 Jun 2019 Results published in the CNS Drugs
- 10 Aug 2017 Safety and efficacy results published in The Lancet.
- 18 Apr 2017 Status changed from active, no longer recruiting to completed.