AN EXPANDED ACCESS PROTOCOL FOR SEBELIPASE ALFA FOR PATIENTS WITH LYSOSOMAL ACID LIPASE DEFICIENCY
Latest Information Update: 03 Nov 2023
At a glance
- Drugs Sebelipase alfa (Primary)
- Indications Lysosomal storage diseases
- Focus Expanded access; Therapeutic Use
- Sponsors Alexion AstraZeneca Rare Disease; Synageva BioPharma
Most Recent Events
- 05 Mar 2015 New trial record