Compassionate Use of Triheptanoin (UX007) to Treat Citrate Transporter Deficiency
Latest Information Update: 06 Nov 2021
At a glance
- Drugs Triheptanoin (Primary)
- Indications Lipid metabolism disorders
- Focus Expanded access; Therapeutic Use
- 27 Jan 2016 Status changed from recruiting to completed, according to ClinicalTrials.gov record.
- 24 Jul 2015 New trial record