Trial Profile

A Prospective, Observational Study of Patients With Fabry Disease (US Specific)

Status: Not yet recruiting

Phase of Trial: Phase IV

Latest Information Update: 09 Apr 2025

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At a glance

Drugs Migalastat (Primary) ; Enzyme replacements
Indications Fabry's disease
Focus Therapeutic Use
Sponsors Amicus Therapeutics

Most Recent Events

02 Apr 2025 Status changed from planning to not yet recruiting.
10 Aug 2018 According to an Amicus Therapeutics media release, as a condition of accelerated approval, the company will study Galafold in this confirmatory phase 4 study.
17 Sep 2015 New trial record

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