Trial Profile

Intrathecal 2-hydroxypropyl-beta-cyclodextrin (HPBCD) therapy in adult-onset Niemann-Pick disease type C (NPC)

Status: Active, no longer recruiting

Phase of Trial: Phase II

Latest Information Update: 16 Jun 2022

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At a glance

Drugs Hydroxypropyl betadex (Primary)
Indications Niemann-Pick disease type C
Focus Therapeutic Use

Most Recent Events

09 Dec 2015 New trial record

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