A Phase I/II Study to Evaluate the Safety and PK of iv Trappsol Cyclo (HP-β-CD) in Patients With Niemann-Pick Disease Type C NPC-1 and the Pharmacodynamic Effects of Treatment Upon Markers of Cholesterol Metabolism and Clinical Outcomes
Phase of Trial: Phase I/II
Latest Information Update: 20 Apr 2018
At a glance
- Drugs Hydroxypropyl betadex (Primary)
- Indications Niemann-Pick disease type C
- Focus Pharmacokinetics; Therapeutic Use
- Sponsors CTD Holdings
- 13 Apr 2018 Planned End Date changed from 1 Dec 2018 to 1 Aug 2019.
- 13 Apr 2018 Planned primary completion date changed from 1 Mar 2018 to 1 Aug 2019.
- 29 Mar 2018 According to a CTD Holdings media release, initial review of safety data for this study has been completed.