Trial Profile

A Phase I / 2, Multicenter, Open-label, Single-dose, Dose-ranging Study to Assess the Safety and Tolerability of SB-318, a rAAV2/6-based Gene Transfer in Subjects With Mucopolysaccharidosis I (MPS I)

Status: Discontinued

Phase of Trial: Phase I/II

Latest Information Update: 30 Jan 2023

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At a glance

Drugs SB 318 (Primary)
Indications Mucopolysaccharidosis I
Focus Adverse reactions
Acronyms EMPOWERS
Sponsors Sangamo Therapeutics

Most Recent Events

01 Dec 2021 Status changed from active, no longer recruiting to discontinued.
21 Oct 2021 Planned primary completion date changed from 31 Oct 2021 to 30 Nov 2021.
16 Sep 2021 Planned primary completion date changed from 1 Jun 2021 to 31 Oct 2021.

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