The Effectiveness of High-Dose Synthetic BH4 (Saproterin Dihydrochloride or "Kuvan") in Amish PKU Patients
Latest Information Update: 29 Apr 2022
At a glance
- Drugs Sapropterin (Primary)
- Indications Phenylketonuria
- Focus Therapeutic Use
Most Recent Events
- 26 Apr 2022 Status changed from recruiting to completed.
- 30 Nov 2017 Planned End Date changed from 1 Aug 2016 to 1 Aug 2018.
- 30 Nov 2017 Planned primary completion date changed from 1 Aug 2016 to 1 Jun 2018.