Trial Profile

Clinical Pilot Study of Autologous Stem Cell Transplantation of Cluster of Differentiation 34 Positive (CD34+) Cells Engineered to Express Alpha-Galactosidase A in Patients With Fabry Disease

Status: Completed

Phase of Trial: Phase I

Latest Information Update: 22 Apr 2024

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At a glance

Drugs AVR RD 01 (Primary)
Indications Fabry's disease
Focus Adverse reactions; First in man
Acronyms FACTs

Most Recent Events

16 Apr 2024 Status changed from active, no longer recruiting to completed.
24 Nov 2021 Results published in an AVROBIO Media Release.
24 Nov 2021 According to an AVROBIO media release, data presented at the 14th International Congress of Inborn Errors of Metabolism (ICIEM).

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