CNS Unmet Medical Need in Mucopolysaccharidosis: A Phase 2 Safety and Pharmacokinetics Study of Ataluren (COMPASS)
Latest Information Update: 02 Jul 2019
At a glance
- Drugs Ataluren (Primary)
- Indications Mucopolysaccharidosis I
- Focus Adverse reactions; Pharmacokinetics
- Acronyms COMPASS
- Sponsors PTC Therapeutics
- 29 Jun 2019 Status changed from recruiting to discontinued.
- 11 Mar 2016 New trial record