Trial Profile

A Follow-On Study to Evaluate the Safety of Re-Administration of Adeno-Associated Viral Vector Containing the Gene for Human RPE65 [AAV2-hRPE65v2] to the Contralateral Eye in Subjects With Leber Congenital Amaurosis (LCA) Previously Enrolled in a Phase 1 Study

Status: Active, no longer recruiting

Phase of Trial: Phase I/II

Latest Information Update: 07 May 2025

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At a glance

29 Apr 2025 Planned End Date changed from 1 Jun 2030 to 1 Oct 2027.
29 Apr 2025 Planned primary completion date changed from 1 Mar 2030 to 1 Oct 2027.
10 Mar 2021 Planned End Date changed from 1 Nov 2026 to 1 Jun 2030.

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