Either you have JavaScript disabled or your browser does not support Javascript . To work properly, this page requires JavaScript to be enabled.
How to enable JavaScript in your browser?

Open-label, Single-arm, Multi-center Study of Intracerebral Administration of Adeno-associated Viral (AAV) Serotype rh.10 Carrying Human N-sulfoglucosamine Sulfohydrolase (SGSH) cDNA for Treatment of Mucopolysaccharidosis Type IIIA

Next Previous
X
Search
Trial Profile

Open-label, Single-arm, Multi-center Study of Intracerebral Administration of Adeno-associated Viral (AAV) Serotype rh.10 Carrying Human N-sulfoglucosamine Sulfohydrolase (SGSH) cDNA for Treatment of Mucopolysaccharidosis Type IIIA

Status: Active, no longer recruiting
Phase of Trial: Phase II/III

Latest Information Update: 13 Sep 2023

Price : $35 *
  • Adis is an information provider.
  • Final gross price and currency may vary according to local VAT and billing address.
  • Your purchase entitles you to full access to the information contained in our trial profile at the time of purchase.
  • A link to download a PDF version of the trial profile will be included in your email receipt.

At a glance

  • Drugs Olenasufligene relduparvovec (Primary)
  • Indications Mucopolysaccharidosis III
  • Focus Proof of concept; Registrational; Therapeutic Use
  • Acronyms AAVance
  • Sponsors LYSOGENE

    • Most Recent Events

    • 11 Sep 2023 According to European Clinical Trials Database, study has been suspended in Germany
    • 29 Nov 2022 According to a Lysogene media release, the company has initiated fruitful discussions with regulatory authorities in the European Union in late Q3 2022.
    • 29 Nov 2022 According to a Lysogene media release, the company will complete full analysis and evaluation of the data from the main cohort of AAVance and work with investigators on the future presentation and publication of the results.

You need to be a logged in or subscribed to view this content Request demo

If your organization or you do not have a subscription, try one of the following:
  • Contacting your organization’s admin about adding this content to your AdisInsight subscription
  • Buying a PDF version of any individual profile
  • Request a free trial
If your organization has a subscription, there are several access options, even while working remotely:
  • Working within your organization’s network
  • with username/password or try to via your institution
  • Persisted access using your organization’s identifier stored in your user browser for 90 days
Back to top