Trial Profile

A Two Part Seamless, Multi-Center Randomized, Placebo-Controlled, Double-Blind Study to Investigate the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics and Efficacy of Risdiplam (RO7034067) in Type 2 and 3 Spinal Muscular Atrophy Patients

Status: Completed

Phase of Trial: Phase II/III

Latest Information Update: 19 Mar 2025

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At a glance

17 Mar 2025 According to a Roche media release, company will present new data at the Muscular Dystrophy Association (MDA) conference, 16-19 March, 2025, in Dallas, Texas.
12 Feb 2025 According to Genentech media release, company announced today that the U.S. Food and Drug Administration (FDA) has approved a New Drug Application (NDA) for an Evrysdi (risdiplam) tablet for people living with spinal muscular atrophy (SMA).
23 Oct 2023 Status changed from active, no longer recruiting to completed.

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